Question

Is gene therapy a permanent cure?

Answer 1

Gene therapy:

1. So basically, gene therapy is a method of medical treatment or prevention that just involves the correction of a genetic defect.
2. The first gene treatment approach which is actually known as the gene transfer or gene addition was first created to battle against the illness
3. Further, this inserted a new gene into cells and introduced a non-faulty copy of a gene just to replace the disease-causing altered copy.
4. ADA deficiency is actually an inherited disorder that just damages the immune system and also causes severe combined immunodeficiency.
5. And this ADA deficiency is actually a result of the mutation in the AD genes that code for the Adenosine deaminase enzyme that is just included in the purine metabolism.
6. In this gene therapy, the doctors just inject the vector that carries the gene into the patient.
7. Hence, this gene therapy offers the possibility of a permanent cure and also for any of the more than ten thousand diseases that are just caused by the defect only in a gene.