Question

Which of the following statements regarding gene therapy is/are correct?

• A. It is an application of biotechnology, in which a defective gene is manipulated by introduction of a normal, healthy and functional gene.
• B. The genetic disorders that are being investigated for gene therapy, range from sickle-cell anemia to server combined immuno-deficiency (SCID).
• C. The first clinical gene therapy was given in 1990 to a 4-year old girl with adenosine deaminase (ADA) deficiency.
• D. All of the above
  

Answer 1

The correct option is D All of the above

Gene therapy is a technique for correcting defective genes responsible for disease development. Under intensive investigation are, disease ranging from the rare genetic diseases caused by single mutations like sickle cell anaemia to killer diseases such as server combined immuno-deficiency (SCID). The first clinical gene therapy was given in 1990 to a 4-years old girl with adenosine deaminase (ADA) deficiency. This enzymes is very important for the immune system to function. ADA deficiency can lead to severe combined immuno-deficiency (SCID).

So, the correct answer is 'All of the above'.